发明名称 ADENOVIRAL VECTORS ENCODING ERYTHROPOIETIN AND THEIR USE IN GENE THERAPY
摘要 Helper dependant adenoviral vectors encoding erythropoietin (epo) provide hi gh levels of epo to achieve a long-term therapeutically effective dosage, and allow for repeat administration to patients with disorders such as anaemia o f Chronic Renal Failure (CRF), anaemias due to beta-thalassaemia, and sickle cell anaemia (SCA).
申请公布号 CA2339779(A1) 申请公布日期 2000.02.24
申请号 CA19992339779 申请日期 1999.08.05
申请人 ISTITUTO DI RICERCHE DI BIOLOGIA MOLECOLARE P. ANGELETTI S.P.A. 发明人 LA MONICA, NICOLA;CILIBERTO, GENNARO;SAVINO, ROCCO
分类号 C12N15/09;A61K35/76;A61K38/18;A61K38/22;A61K48/00;A61P7/00;A61P7/06;C07K14/505;C12N7/00;C12R1/93;(IPC1-7):C12N15/64;C12N15/86 主分类号 C12N15/09
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