发明名称 ADENOVIRAL VECTORS ENCODING ERYTHROPOIETIN AND THEIR USE IN GENE THERAPY
摘要 Helper dependant adenoviral vectors encoding erythropoietin (epo) provide high levels of epo to achieve a long-term therapeutically effective dosage, and allow for repeat administration to patients with disorders such as anaemia of Chronic Renal Failure (CRF), anaemias due to beta-thalassaemia, and sickle cell anaemia (SCA).
申请公布号 WO0009713(A1) 申请公布日期 2000.02.24
申请号 WO1999EP05661 申请日期 1999.08.05
申请人 ISTITUTO DI RICERCHE DI BIOLOGIA MOLECOLARE P. ANGELETTI S.P.A.;SAVINO, ROCCO;CILIBERTO, GENNARO;LA MONICA, NICOLA 发明人 SAVINO, ROCCO;CILIBERTO, GENNARO;LA MONICA, NICOLA
分类号 C12N15/09;A61K35/76;A61K38/18;A61K38/22;A61K48/00;A61P7/00;A61P7/06;C07K14/505;C12N7/00;C12R1/93;(IPC1-7):C12N15/64;C12N15/86 主分类号 C12N15/09
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