发明名称 |
ADENOVIRAL VECTORS ENCODING ERYTHROPOIETIN AND THEIR USE IN GENE THERAPY |
摘要 |
Helper dependant adenoviral vectors encoding erythropoietin (epo) provide high levels of epo to achieve a long-term therapeutically effective dosage, and allow for repeat administration to patients with disorders such as anaemia of Chronic Renal Failure (CRF), anaemias due to beta-thalassaemia, and sickle cell anaemia (SCA).
|
申请公布号 |
WO0009713(A1) |
申请公布日期 |
2000.02.24 |
申请号 |
WO1999EP05661 |
申请日期 |
1999.08.05 |
申请人 |
ISTITUTO DI RICERCHE DI BIOLOGIA MOLECOLARE P. ANGELETTI S.P.A.;SAVINO, ROCCO;CILIBERTO, GENNARO;LA MONICA, NICOLA |
发明人 |
SAVINO, ROCCO;CILIBERTO, GENNARO;LA MONICA, NICOLA |
分类号 |
C12N15/09;A61K35/76;A61K38/18;A61K38/22;A61K48/00;A61P7/00;A61P7/06;C07K14/505;C12N7/00;C12R1/93;(IPC1-7):C12N15/64;C12N15/86 |
主分类号 |
C12N15/09 |
代理机构 |
|
代理人 |
|
主权项 |
|
地址 |
|