| 发明名称 |
ADENOASSOCIATED VIRUS VECTORS FOR THE TREATMENT OF MUCOPOLYSACCHARIDOSES |
| 摘要 |
The present invention provides new Adeno-associated virus-derivedvectors and pharmaceutical compositions containing the same for the treatment of lysosomal storage disordersand specially, for the treatment of mucopolysaccharidoses Type II. |
| 申请公布号 |
WO2016193431(A1) |
申请公布日期 |
2016.12.08 |
| 申请号 |
WO2016EP62655 |
申请日期 |
2016.06.03 |
| 申请人 |
LABORATORIOS DEL DR. ESTEVE, S.A.;UNIVERSITAT AUTÓNOMA DE BARCELONA |
发明人 |
BOSCH TUBERT, Maria Fátima;AREBA HAURIGOT, Virginia;MOTAS MALLOL, Sandra |
| 分类号 |
C12N9/16;A61K48/00;C12N15/864 |
主分类号 |
C12N9/16 |
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