发明名称 RNA-GUIDED SYSTEMS FOR IN VIVO GENE EDITING
摘要 Methods of editing target nucleic acids are provided using a guide RNA and a Cas9 protein to excise exons in a target gene and where the edited gene is expressed to produce a truncated polypeptide.
申请公布号 WO2016089866(A1) 申请公布日期 2016.06.09
申请号 WO2015US63181 申请日期 2015.12.01
申请人 PRESIDENT AND FELLOWS OF HARVARD COLLEGE 发明人 WAGERS, AMY J.;TABEBORDBAR, MOHAMMADSHARIF;CHEW, WEI LEONG;CHURCH, GEORGE M.
分类号 C12N15/00;A61K48/00;C12N9/10;C12N15/07;C12N15/87 主分类号 C12N15/00
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