发明名称 |
Gene repair involving in vivo excision of targeting DNA |
摘要 |
Methods of modifying, repairing, attenuating and inactivating a gene or other chromosomal DNA in a cell are disclosed. Also disclosed are methods of treating or prophylaxis of a genetic disease in an individual in need thereof.
|
申请公布号 |
US2002110898(A1) |
申请公布日期 |
2002.08.15 |
申请号 |
US20010922495 |
申请日期 |
2001.08.03 |
申请人 |
THE CHILDREN'S MEDICAL CENTER CORPORATION |
发明人 |
CHOULIKA ANDRE;MULLIGAN RICHARD C. |
分类号 |
C12N15/09;A61K31/711;A61K35/76;A61K48/00;A61P43/00;C12N5/10;C12N15/90;(IPC1-7):C12N1/20 |
主分类号 |
C12N15/09 |
代理机构 |
|
代理人 |
|
主权项 |
|
地址 |
|