| 发明名称 |
ADENO-ASSOCIATED VIRUS FACTOR VIII VECTORS |
| 摘要 |
The invention provides improved adeno-associated virus (AAV) Factor VIII (FVIII) vectors, including AAV FVIII vectors that produce a functional Factor VIII polypeptide and AAV FVIII vectors with high expression activity. |
| 申请公布号 |
EP3044231(A1) |
申请公布日期 |
2016.07.20 |
| 申请号 |
EP20140771729 |
申请日期 |
2014.09.10 |
| 申请人 |
BIOMARIN PHARMACEUTICAL INC.;UNIVERSITY COLLEGE LONDON |
发明人 |
COLOSI, PETER CAMERON;NATHWANI, AMIT;MCINTOSH, JENNY;TUDDENHAM, EDWARD |
| 分类号 |
C07K14/755;A61K48/00;C12N15/86 |
主分类号 |
C07K14/755 |
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