| 发明名称 |
COMPOSITIONS FOR TREATING DISEASES RELATED TO LYSOME DISORDERS |
| 摘要 |
The invention relates to a pharmaceutical composition comprising a pharmacological chaperone and coenzyme Q10 (CoQ), and the use thereof for treating a disease caused by mutations in the gene GBA1, particularly for treating Gaucher disease. |
| 申请公布号 |
WO2016162588(A1) |
申请公布日期 |
2016.10.13 |
| 申请号 |
WO2016ES70244 |
申请日期 |
2016.04.08 |
| 申请人 |
CONSEJO SUPERIOR DE INVESTIGACIONES CIENTÍFICAS (CSIC);UNIVERSIDAD DE SEVILLA;UNIVERSIDAD PABLO DE OLAVIDE |
发明人 |
GARCÍA FERNÁNDEZ, José Manuel;ORTIZ MELLET, Carmen;SÁNCHEZ ALCÁZAR, José Antonio;DE LA MATA FERNÁNDEZ, Mario |
| 分类号 |
A61K31/22;A61K31/455;A61P31/00 |
主分类号 |
A61K31/22 |
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