发明名称 COMPOSITIONS FOR MODULATING C9ORF72 EXPRESSION
摘要 Disclosed herein are compositions and methods for reducing expression of C90RF72 mRNA and protein in an animal. Such methods are useful to treat, prevent, ameliorate, or slow progression of neurodegenerative diseases in an individual in need thereof.
申请公布号 WO2016168592(A2) 申请公布日期 2016.10.20
申请号 WO2016US27747 申请日期 2016.04.15
申请人 IONIS PHARMACEUTICALS, INC. 发明人 RIGO, Frank
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