| 发明名称 |
PRODUCTION OF LARGE-SIZED MICRODYSTROPHINS IN AN AAV-BASED VECTOR CONFIGURATION |
| 摘要 |
An adeno-associated viral (AAV) vector containing an expression construct, wherein: - the expression construct comprises a nucleic acid sequence which encodes a microdystrophin (MD); and - the nucleic acid sequence encoding the MD has a size of at least 4,1 kb. |
| 申请公布号 |
WO2016177911(A1) |
申请公布日期 |
2016.11.10 |
| 申请号 |
WO2016EP60350 |
申请日期 |
2016.05.09 |
| 申请人 |
ROYAL HOLLOWAY & BEDFORD NEW COLLEGE |
发明人 |
DICKSON, George |
| 分类号 |
C07K14/47;A61K38/00;C12N15/86 |
主分类号 |
C07K14/47 |
| 代理机构 |
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