| 发明名称 |
MEANS AND METHODS FOR COUNTERACTING MUSCLE DISORDERS |
| 摘要 |
PROBLEM TO BE SOLVED: To provide means and methods for alleviating one or more symptom(s) of Duchenne Muscular Dystrophy and/or Becker Muscular Dystrophy.SOLUTION: A composition is a combination of the following: a compound for providing an individual with a functional dystrophin protein; and a secondary compound for reducing inflammation and/or for improving calcium homeostasis, muscle fiber function, integrity and/or survival. The combination is used as a drug.SELECTED DRAWING: None |
| 申请公布号 |
JP2016033140(A) |
申请公布日期 |
2016.03.10 |
| 申请号 |
JP20150219928 |
申请日期 |
2015.11.09 |
| 申请人 |
ACADEMISCH ZIEKENHUIS LEIDEN;BIOMARIN TECHNOLOGIES B V |
发明人 |
JOSEPHUS JOHANNES DE KIMPE;PLATENBURG GERARDUS JOHANNES;JUDITH CHRISTINA THEODORA VAN DEUTEKOM;ANNEMIEKE AARTSMA-RUS;GARRIT-JAN BOUDEWIJN VAN OMMEN |
| 分类号 |
A61K45/06;A61K31/198;A61K31/4178;A61K31/4245;A61K31/573;A61K31/7036;A61K31/7088;A61K31/7105;A61K31/787;A61K48/00;A61P3/14;A61P21/00;A61P21/04;A61P29/00;A61P39/06;A61P43/00;C12N5/16;C12N15/09;C12N15/113;C12P21/02 |
主分类号 |
A61K45/06 |
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