The present invention provides a pharmaceutical composition which causes skipping of the 53rd exon in the human dystrophin gene with a high efficiency. The present invention provides an oligomer which efficiently enables to cause skipping of the 53rd exon in the human dystrophin gene.
申请公布号
HRP20160336(T1)
申请公布日期
2016.04.22
申请号
HR2016P000336T
申请日期
2016.04.04
申请人
Nippon Shinyaku Co., Ltd.;National Center of Neurology and Psychiatry
