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发明名称
COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TRANSTHYRETIN
摘要
The invention relates to a double-stranded ribonucleic acid (dsRNA) targeting a transthyretin (TTR) gene, and methods of using the dsRNA to inhibit expression of TTR.
申请公布号
HK1216652(A1)
申请公布日期
2016.11.25
申请号
HK20160104672
申请日期
2016.04.22
申请人
Alnylam Pharmaceuticals Inc.
发明人
Sah, Dinah Wen-yee;Hinkle, Gregory;Alvarez, Rene;Milstein, Stuart;Chen, Qingmin
分类号
C12N;A61K
主分类号
C12N
代理机构
代理人
主权项
地址
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