发明名称 |
METHOD OF INCREASING FUNCTION OF AAV VECTOR |
摘要 |
PROBLEM TO BE SOLVED: To provide an adeno-associated virus which can effectively deliver a transgene.SOLUTION: An AAV includes an AAVrh.20 capsid, a minigene comprising AAV inverted terminal repeat sequences (ITRs) and a foreign gene functionally coupled to a regulatory sequence that controls expression in a host cell.SELECTED DRAWING: None |
申请公布号 |
JP2016168047(A) |
申请公布日期 |
2016.09.23 |
申请号 |
JP20160093699 |
申请日期 |
2016.05.09 |
申请人 |
TRUSTEES OF THE UNIV OF PENNSYLVANIA |
发明人 |
VANDENBERGHE LUK;GAO GUANGPING;WILSON JAMES M |
分类号 |
C12N7/01;A61K35/761;A61K39/00;C12N1/15;C12N1/19;C12N1/21;C12N5/10;C12N15/09 |
主分类号 |
C12N7/01 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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