发明名称 METHOD OF INCREASING FUNCTION OF AAV VECTOR
摘要 PROBLEM TO BE SOLVED: To provide an adeno-associated virus which can effectively deliver a transgene.SOLUTION: An AAV includes an AAVrh.20 capsid, a minigene comprising AAV inverted terminal repeat sequences (ITRs) and a foreign gene functionally coupled to a regulatory sequence that controls expression in a host cell.SELECTED DRAWING: None
申请公布号 JP2016168047(A) 申请公布日期 2016.09.23
申请号 JP20160093699 申请日期 2016.05.09
申请人 TRUSTEES OF THE UNIV OF PENNSYLVANIA 发明人 VANDENBERGHE LUK;GAO GUANGPING;WILSON JAMES M
分类号 C12N7/01;A61K35/761;A61K39/00;C12N1/15;C12N1/19;C12N1/21;C12N5/10;C12N15/09 主分类号 C12N7/01
代理机构 代理人
主权项
地址