发明名称 |
ANTISENSE NUCLEIC ACIDS |
摘要 |
Provided is a drug that allows highly-efficient skipping of exon 51 in the human dystrophin gene. The present invention provides an antisense oligomer which enables exon 51 in the human dystrophin gene to be skipped. |
申请公布号 |
SG11201607095R(A) |
申请公布日期 |
2016.10.28 |
申请号 |
SG11201607095R |
申请日期 |
2015.03.11 |
申请人 |
NIPPON SHINYAKU CO., LTD.;NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY |
发明人 |
WAKAYAMA TATSUSHI;SEO HARUNA;SATOU YOUHEI;TAKEDA SHIN'ICHI;NAGATA TETSUYA |
分类号 |
C12N15/09;A61K31/711;A61K31/712;A61K31/7125;A61P21/00;C12N15/113 |
主分类号 |
C12N15/09 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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