发明名称 ANTISENSE NUCLEIC ACIDS
摘要 Provided is a drug that allows highly-efficient skipping of exon 51 in the human dystrophin gene. The present invention provides an antisense oligomer which enables exon 51 in the human dystrophin gene to be skipped.
申请公布号 SG11201607095R(A) 申请公布日期 2016.10.28
申请号 SG11201607095R 申请日期 2015.03.11
申请人 NIPPON SHINYAKU CO., LTD.;NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY 发明人 WAKAYAMA TATSUSHI;SEO HARUNA;SATOU YOUHEI;TAKEDA SHIN'ICHI;NAGATA TETSUYA
分类号 C12N15/09;A61K31/711;A61K31/712;A61K31/7125;A61P21/00;C12N15/113 主分类号 C12N15/09
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