发明名称 |
COMPOSITIONS AND METHODS FOR THE TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS |
摘要 |
The present invention relates to compositions and methods for the treatment of nucleotide repeat expansion disorders such as myotonic dystrophy. |
申请公布号 |
WO2016174056(A1) |
申请公布日期 |
2016.11.03 |
申请号 |
WO2016EP59346 |
申请日期 |
2016.04.27 |
申请人 |
GENETHON;INSERM (INSTITUT NATIONAL DE LA SANTÉ ET DE LA RECHERCHE MÉDICALE);UNIVERSITE D'EVRY VAL D'ESSONNE |
发明人 |
BUJ BELLO, Ana Maria;LO SCRUDATO, Mirella |
分类号 |
C12N15/10;C12N15/11;C12N15/63 |
主分类号 |
C12N15/10 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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