INTRA-AMNIOTIC ADMINISTRATION OF PROTEINS FOR THE TREATMENT OF ECTODERMAL DYSPLASIAS

摘要

The invention relates to methods for the intra-amniotic administration of EDA agonists, in particular EDI200. Use of the methods described allow for the design of targeted therapeutic dosing and administration regimens in order to correct or alter abnormal phenotypes associated with ectodermal dysplasias, in particular, XLHED.