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发明名称
DELIVERY METHODS AND COMPOSITIONS FOR NUCLEASE-MEDIATED GENOME ENGINEERING IN HEMATOPOIETIC STEM CELLS
摘要
The present disclosure is in the field of genome engineering, particularly targeted modification of the genome of a hematopoietic cell.
申请公布号
EP3057432(A4)
申请公布日期
2017.04.05
申请号
EP20140853797
申请日期
2014.10.16
申请人
Sangamo BioSciences, Inc.;Ospedale San Raffaele S.r.l.;Fondazione Telethon
发明人
GENOVESE, Pietro;GREGORY, Philip D.;HOLMES, Michael C.;LOMBARDO, Angelo Leone;NALDINI, Luigi
分类号
A01N63/00;C07H21/04;C12N5/00;C12N15/00;C12N15/87;C12P21/04
主分类号
A01N63/00
代理机构
代理人
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