| 发明名称 |
CRISPR/CAS-RELATED METHODS AND COMPOSITIONS FOR TREATING USHER SYNDROME AND RETINITIS PIGMENTOSA |
| 摘要 |
CRISPR/Cas-related compositions and methods for treatment of Usher Syndrome and/or Retinitis Pigmentosa are disclosed herein. |
| 申请公布号 |
US2017073674(A1) |
申请公布日期 |
2017.03.16 |
| 申请号 |
US201515123576 |
申请日期 |
2015.03.05 |
| 申请人 |
EDITAS MEDICINE, INC. |
发明人 |
MAEDER Morgan L.;BUMCROT David A. |
| 分类号 |
C12N15/113;C12N9/22;C12N7/00;A61K38/46;A61K47/26 |
主分类号 |
C12N15/113 |
| 代理机构 |
|
代理人 |
|
| 主权项 |
1. A gRNA molecule comprising a targeting domain which is complementary with a target domain from the USH2A gene. |
| 地址 |
Cambridge MA US |
