发明名称 |
METHODS FOR TREATMENT OF POLYCYSTIC KIDNEY DISEASE |
摘要 |
Provided herein are methods for the treatment of polycystic kidney disease, including autosomal dominant polycystic kidney disease, using modified oligonucleotides targeted to miR-17. |
申请公布号 |
WO2017035319(A1) |
申请公布日期 |
2017.03.02 |
申请号 |
WO2016US48603 |
申请日期 |
2016.08.25 |
申请人 |
REGULUS THERAPEUTICS INC.;BOARD OF REGENTS OF THE UNIVERSITY OF TEXAS SYSTEM |
发明人 |
ANDROSAVICH, John R.;CHAU, B. Nelson;PATEL, Vishal D. |
分类号 |
A61K31/7088;A61K45/06;A61P13/12;C12N15/113 |
主分类号 |
A61K31/7088 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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