发明名称 METHODS FOR TREATMENT OF POLYCYSTIC KIDNEY DISEASE
摘要 Provided herein are methods for the treatment of polycystic kidney disease, including autosomal dominant polycystic kidney disease, using modified oligonucleotides targeted to miR-17.
申请公布号 WO2017035319(A1) 申请公布日期 2017.03.02
申请号 WO2016US48603 申请日期 2016.08.25
申请人 REGULUS THERAPEUTICS INC.;BOARD OF REGENTS OF THE UNIVERSITY OF TEXAS SYSTEM 发明人 ANDROSAVICH, John R.;CHAU, B. Nelson;PATEL, Vishal D.
分类号 A61K31/7088;A61K45/06;A61P13/12;C12N15/113 主分类号 A61K31/7088
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