| 发明名称 |
Methods and materials for activating an internal ribosome entry site in exon 5 of the DMD gene |
| 摘要 |
The present invention relates to the delivery of oligomers for treating patients with a 5' mutation in their |
| 申请公布号 |
AU2015301978(A1) |
申请公布日期 |
2017.03.02 |
| 申请号 |
AU20150301978 |
申请日期 |
2015.08.07 |
| 申请人 |
Research Institute at Nationwide Children's Hospital;University Of Western Australia |
发明人 |
Flanigan, Kevin;Wein, Nicolas;Wilton, Steven |
| 分类号 |
C12N15/66;A61K31/7088;A61P21/00;C07H21/02;C07H21/04;C12N15/63 |
主分类号 |
C12N15/66 |
| 代理机构 |
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代理人 |
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| 地址 |
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