发明名称 |
METHODS AND COMPOSITIONS FOR THE SPECIFIC INHIBITION OF ANTITHROMBIN 3 (AT3) BY DOUBLE-STRANDED RNA |
摘要 |
This invention relates to compounds, compositions, and methods useful for reducing AT3 target RNA and protein levels via use of dsRNAs, e.g., Dicer substrate siRNA (DsiRNA) agents. |
申请公布号 |
WO2016183009(A3) |
申请公布日期 |
2017.02.16 |
申请号 |
WO2016US31471 |
申请日期 |
2016.05.09 |
申请人 |
DICERNA PHARMACEUTICALS, INC. |
发明人 |
BROWN, Bob, D.;DUDEK, Henryk, T. |
分类号 |
A61K31/7088;A61K31/713;A61P7/04;C07K14/81;C12N15/113 |
主分类号 |
A61K31/7088 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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