发明名称 |
CRISPR/CAS-RELATED METHODS AND COMPOSITIONS FOR TREATING PRIMARY OPEN ANGLE GLAUCOMA |
摘要 |
CRISPR/CAS-related compositions and methods for treatment of Primary Open Angle Glaucoma (POAG) are disclosed. |
申请公布号 |
US2017029850(A1) |
申请公布日期 |
2017.02.02 |
申请号 |
US201515300991 |
申请日期 |
2015.04.01 |
申请人 |
EDITAS MEDICINE, INC. |
发明人 |
MAEDER Morgan L.;BUMCROT David A. |
分类号 |
C12N15/90;A61K47/48;A61K48/00;A61K38/46;C12N15/11;C12N9/22 |
主分类号 |
C12N15/90 |
代理机构 |
|
代理人 |
|
主权项 |
1. A gRNA molecule comprising a targeting domain which is complementary with a target domain from the MYOC gene. |
地址 |
Cambridge MA US |