| 发明名称 |
CRISPR/CAS-RELATED METHODS AND COMPOSITIONS FOR TREATING CYSTIC FIBROSIS |
| 摘要 |
CRISPR/CAS-related compositions and methods for treatment of Cystic Fibrosis (CF). |
| 申请公布号 |
US2017022507(A1) |
申请公布日期 |
2017.01.26 |
| 申请号 |
US201615288475 |
申请日期 |
2016.10.07 |
| 申请人 |
EDITAS MEDICINE, INC. |
发明人 |
Reyon Deepak;Maeder Morgan L.;Friedland Ari E.;Welstead Grant G.;Bumcrot David A. |
| 分类号 |
C12N15/113;C12N9/22 |
主分类号 |
C12N15/113 |
| 代理机构 |
|
代理人 |
|
| 主权项 |
1. A CRISPR/Cas system comprising: a gRNA molecule and a Cas9 molecule, wherein the system is configured to correct a mutation at F508 of a cystic fibrosis transmembrane conductance regulator (CFTR) protein. |
| 地址 |
Cambridge MA US |
