发明名称 |
COMPOSITIONS FOR INHIBITING DUX4 GENE EXPRESSION AND USES THEREOF |
摘要 |
The present invention is directed to compounds, compositions, and methods useful for modulating DUX4 mRNA or protein expression using gene silencing compounds comprising two or more single stranded antisense oligonucleotides that are linked through their 5 '-ends to allow the presence of two or more accessible 3 '-ends. |
申请公布号 |
WO2017007886(A2) |
申请公布日期 |
2017.01.12 |
申请号 |
WO2016US41261 |
申请日期 |
2016.07.07 |
申请人 |
IDERA PHARMACEUTICALS, INC. |
发明人 |
AGRAWAL, Sudhir;BHAGA, Lakshmi;ZHU, Fu-Gang |
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