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发明名称
NUCLEIC ACID MOLECULES TARGETING SUPEROXIDE DISMUTASE 1 (SOD1)
摘要
Aspects of the invention relate to methods for treating ALS comprising administering to a subject in need thereof a therapeutically effective amount of a nucleic acid molecule that is directed against a gene encoding superoxide dismutase 1 (SOD1).
申请公布号
WO2017007813(A1)
申请公布日期
2017.01.12
申请号
WO2016US41095
申请日期
2016.07.06
申请人
RXI PHARMACEUTICALS CORPORATION
发明人
CARDIA, James;BYRNE, Michael;BULOCK, Karen, G.;PAVCO, Pamela, A.;LIBERTINE, Lyn
分类号
A61K31/713;A61P25/28;C07H21/02;C12N15/113
主分类号
A61K31/713
代理机构
代理人
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