发明名称 |
AGE-RELATED MACULAR DEGENERATION TREATMENT |
摘要 |
This invention is directed to an RNA interference (RNAi) agent and the use of that RNAi agent to treat Age-related Macular Degeneration, as well as pharmaceutical compositions containing the RNAi agents of the invention. The RNAi agent is a DNA-directed RNA interference (ddRNAi) agent (being an RNA molecule), together with an expression cassette or construct to express that agent in a cell (including in vivo), for inhibiting, preventing or reducing expression of an AMD associated gene. Preferably that AMD associated gene is one that is associated with wet AMD. |
申请公布号 |
EP2943571(A4) |
申请公布日期 |
2016.11.30 |
申请号 |
EP20140737958 |
申请日期 |
2014.01.08 |
申请人 |
BENITEC BIOPHARMA LIMITED |
发明人 |
SUHY, DAVID;MAO, TIN;KAO, SHIH-CHU |
分类号 |
C12N15/113 |
主分类号 |
C12N15/113 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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