发明名称 LIVER SPECIFIC DELIVERY OF MESSENGER RNA
摘要 Disclosed herein are compositions and methods of modulating the expression of gene or the production of a protein by transfecting target cells with nucleic acids. The compositions disclosed herein demonstrate a high transfection efficacy and are capable of ameliorating diseases associated with protein or enzyme deficiencies.
申请公布号 US2016287725(A1) 申请公布日期 2016.10.06
申请号 US201615092226 申请日期 2016.04.06
申请人 Shire Human Genetic Therapies, Inc. 发明人 DeRosa Frank;Heartlein Michael
分类号 A61K48/00;C07J43/00 主分类号 A61K48/00
代理机构 代理人
主权项
地址 Lexington MA US