发明名称 OLIGONUCLEOTIDE COMPOUNDS FOR TARGETING HUNTINGTIN MRNA
摘要 This disclosure relates to novel huntingtin targets. Novel oligonucleotides for the treatment of Huntington's disease are also provided.
申请公布号 WO2016161374(A1) 申请公布日期 2016.10.06
申请号 WO2016US25722 申请日期 2016.04.01
申请人 UNIVERSITY OF MASSACHUSETTS 发明人 KHVOROVA, Anastasia;ARONIN, Neil;ALTERMAN, Julia
分类号 C12N15/113;A61K31/713;A61P25/14 主分类号 C12N15/113
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