发明名称 METHODS AND COMPOSITIONS FOR REGULATION OF METABOLIC DISORDERS
摘要 Cells and methods of using these cells for expressing a transgene expressing a protein that is aberrantly expressed in a metabolic disorders from a safe harbor locus.
申请公布号 EP2929017(A4) 申请公布日期 2016.09.28
申请号 EP20130859888 申请日期 2013.12.04
申请人 SANGAMO BIOSCIENCES, INC.;THE CHILDREN'S HOSPITAL OF PHILADELPHIA 发明人 GREGORY, PHILIP D.;HIGH, KATHERINE A.
分类号 C12N5/10 主分类号 C12N5/10
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