| 发明名称 |
REDUCING NONSENSE-MEDIATED MRNA DECAY |
| 摘要 |
The present disclosure relates to compositions and methods for inhibiting nonsense-mediated mRNA decay in a gene-specific manner, for example in the treatment of diseases or disorders caused by nonsense mutations. |
| 申请公布号 |
EP3041958(A1) |
申请公布日期 |
2016.07.13 |
| 申请号 |
EP20140842672 |
申请日期 |
2014.09.04 |
| 申请人 |
COLD SPRING HARBOR LABORATORY |
发明人 |
KRAINER, ADRIAN;AZNAREZ, ISABEL;NOMAKUCHI, TOMOKI |
| 分类号 |
C12Q1/68;A61K31/7088;C12N15/113 |
主分类号 |
C12Q1/68 |
| 代理机构 |
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| 地址 |
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