| 发明名称 |
Methods and compositions for the specific inhibition of transthyretin (TTR) by double-stranded RNA |
| 摘要 |
This invention relates to compounds, compositions, and methods useful for reducing transthyretin (TTR) target RNA and protein levels via use of dsRNAs, e.g., Dicer substrate siRNA (DsiRNA) agents. |
| 申请公布号 |
AU2014360314(A1) |
申请公布日期 |
2016.06.30 |
| 申请号 |
AU20140360314 |
申请日期 |
2014.12.05 |
| 申请人 |
DICERNA PHARMACEUTICALS, INC. |
发明人 |
BROWN, BOD D.;DUDEK, HENRYK T. |
| 分类号 |
C12N15/113;A61K31/7088;C12Q1/68 |
主分类号 |
C12N15/113 |
| 代理机构 |
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代理人 |
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