ASSAYS FOR DIAGNOSING AND EVALUATING TREATMENT OPTIONS FOR FABRY DISEASE
摘要
DGJ for use in the treatment of Fabry disease, characterised in that the DGJ is administered to a Fabry disease patient in a predetermined amount at a predetermined frequency.
申请公布号
HK1129458(A1)
申请公布日期
2016.05.27
申请号
HK20090107461
申请日期
2009.08.14
申请人
AMICUS THERAPEUTICS INC.
发明人
KANESKI, CHRISTINE;SHIN, SANG-HOON;MURRAY, GARY;LUDWIG, KARIN;LOCKHART, DAVID;CASTELLI, JEFF