发明名称 ASSAYS FOR DIAGNOSING AND EVALUATING TREATMENT OPTIONS FOR FABRY DISEASE
摘要 DGJ for use in the treatment of Fabry disease, characterised in that the DGJ is administered to a Fabry disease patient in a predetermined amount at a predetermined frequency.
申请公布号 HK1129458(A1) 申请公布日期 2016.05.27
申请号 HK20090107461 申请日期 2009.08.14
申请人 AMICUS THERAPEUTICS INC. 发明人 KANESKI, CHRISTINE;SHIN, SANG-HOON;MURRAY, GARY;LUDWIG, KARIN;LOCKHART, DAVID;CASTELLI, JEFF
分类号 G01N 主分类号 G01N
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