发明名称 |
Antisense molecules and methods for treating pathologies |
摘要 |
H:/ft/interwoven/NRPortbl/DCC/FMT/l0103426_ .docx-6/05/2016 An antisense molecule capable of binding to a selected target site to induce exon skipping in the dystrophin gene, as set forth in SEQ ID NO: 1 to 59. |
申请公布号 |
AU2016202924(A1) |
申请公布日期 |
2016.05.26 |
申请号 |
AU20160202924 |
申请日期 |
2016.05.06 |
申请人 |
THE UNIVERSITY OF WESTERN AUSTRALIA |
发明人 |
WILTON, STEPHEN;FLETCHER, SUE;ADAMS, ABBIE;MELONI, PENNY |
分类号 |
C12N15/113;A61K31/7088;A61K31/712;A61K48/00;A61P21/00 |
主分类号 |
C12N15/113 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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