CYCLODEXTRIN FOR THE TREATMENT OF LYSOSOMAL STORAGE DISEASES
摘要
The invention provides for methods of treating lysosomal storage disorders and/or reduction of non-cholesterol lipids, using cyclodextrin compounds, including in combination with other therapeutics, including vitamin E.
申请公布号
HK1210960(A1)
申请公布日期
2016.05.13
申请号
HK20150111861
申请日期
2015.12.02
申请人
THE U.S.A. AS REPRESENTED BY THE SECRETARY DEPARTM
发明人
MCKEW, JOHN;ZHENG, WEI;XU, MIAO;SWAROOP, MANJU;MARUGAN, JUAN, J.