发明名称 COMPOSITIONS AND METHODS OF TREATING USHER SYNDROME III
摘要 An isolated polynucleotide includes a nucleic acid sequence that includes a cDNA coding sequence of a clarin-1 gene and a 3'UTR nucleic acid that is derived from the 3'UTR of the clarin-1 gene. The 3'UTR nucleic acid can enhance expression of clarin-1 in a cell transfected with the polynucleotide compared to a cell transfected with a similar polynucleotide devoid of the 3'UTR nucleic acid.
申请公布号 WO2016073900(A1) 申请公布日期 2016.05.12
申请号 WO2015US59546 申请日期 2015.11.06
申请人 CASE WESTERN RESERVE UNIVERSITY 发明人 ALAGRAMAM, KUMAR N.
分类号 A61K31/7088 主分类号 A61K31/7088
代理机构 代理人
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