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发明名称
GLUCOSYLCERAMIDE SYNTHASE INHIBITORS
摘要
The invention relates to inhibitors of glucosylceramide synthase (GCS) useful for the treatment metabolic diseases, such as lysosomal storage diseases, either alone or in combination with enzyme replacement therapy, and for the treatment of cancer.
申请公布号
SG10201602022U(A)
申请公布日期
2016.04.28
申请号
SG10201602022U
申请日期
2012.03.16
申请人
GENZYME CORPORATION
发明人
BOURQUE, ELYSE;CELATKA, CASSANDRA;HIRTH, BRADFORD;METZ, MARKUS;ZHAO, ZHONG;SKERLJ, RENATO;XIANG, YIBIN;JANCISICS, KATHERINE;MARSHALL, JOHN;CHENG, SENG;SCHEULE, RONALD;CABRERA-SALAZAR, MARIO;GOOD, ANDREW
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