发明名称 Compositions and methods for inhibiting expression of the ALAS1 gene
摘要 The invention relates to double-stranded ribonucleic acid (dsRNA) compositions targeting the ALAS1 gene, and methods of using such dsRNA compositions to alter (e.g., inhibit) expression of ALAS1.
申请公布号 AU2014331604(A1) 申请公布日期 2016.04.21
申请号 AU20140331604 申请日期 2014.10.03
申请人 ALNYLAM PHARMACEUTICALS, INC.;ICAHN SCHOOL OF MEDICINE AT MOUNT SINAI 发明人 BETTENCOURT, BRIAN;FITZGERALD, KEVIN;QUERBES, WILLIAM;DESNICK, ROBERT J.;YASUDA, MAKIKO
分类号 C12N15/113;A61K31/7088;A61K31/713;A61P3/00 主分类号 C12N15/113
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