Certain embodiments of the present invention provide a method for treating or preventing juvenile neuronal ceroid lipofuscinosis (JNCL) in an animal comprising administering CBX, GRA, or GZA to the animal.
申请公布号
EP2996684(A1)
申请公布日期
2016.03.23
申请号
EP20140764138
申请日期
2014.03.17
申请人
UNIVERSITY OF IOWA RESEARCH FOUNDATION;BOARD OF REGENTS OF THE UNIVERSITY OF NEBRASKA
发明人
DAVIDSON, BEVERLY L.;STEIN, COLLEEN S.;SCHULTZ, MARK;TECEDOR, LUIS;KIELIAN, TAMMY L.