发明名称 TREATMENT OPTIONS FOR FABRY DISEASE
摘要 DGJ for use in the treatment of Fabry disease, characterised in that the DGJ is administered to a Fabry disease patient in a predetermined amount at a predetermined frequency.
申请公布号 EP2787345(B1) 申请公布日期 2016.02.24
申请号 EP20140168748 申请日期 2007.05.16
申请人 AMICUS THERAPEUTICS, INC.;NATIONAL INSTITUTES OF HEALTH 发明人 LOCKHART, DAVID;CASTELLI, JEFF
分类号 G01N33/53;A61K31/435;G01N33/567;G01N33/573 主分类号 G01N33/53
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