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发明名称
THERAPEUTIC RETROVIRAL VECTORS FOR GENE THERAPY
摘要
Retroviral gene therapy vectors that are optimized for erythroid specific expression and treatment of hemoglobinopathic conditions are disclosed.
申请公布号
US2016022839(A1)
申请公布日期
2016.01.28
申请号
US201514700021
申请日期
2015.04.29
申请人
BLUEBIRD BIO, INC. ;MASSACHUSETTS INSTITUTE OF TECHNOLOGY
发明人
LEBOULCH Philippe Louis;PAWLIUK Robert;WESTERMAN Karen
分类号
A61K48/00;A61K38/42
主分类号
A61K48/00
代理机构
代理人
主权项
地址
Cambridge MA US
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