发明名称 |
ANTISENSE NUCLEIC ACID |
摘要 |
Provided is a drug that provides highly efficient exon skipping. The present invention provides an antisense oligomer having at least two unit oligomers linked that target arrays that are do not continue on from or overlap with each other within the same exon. |
申请公布号 |
WO2015194520(A1) |
申请公布日期 |
2015.12.23 |
申请号 |
WO2015JP67238 |
申请日期 |
2015.06.16 |
申请人 |
NIPPON SHINYAKU CO., LTD.;NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY |
发明人 |
WATANABE NAOKI;TONE YUUICHIROU;TAKEDA SHIN'ICHI;NAGATA TETSUYA |
分类号 |
C12N15/113;A61K31/712;A61K31/7125;A61K48/00;A61P21/04 |
主分类号 |
C12N15/113 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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