| 摘要 |
Methods and compositions useful in the treatment or prevention of lysosomal storage diseases, such as Pompe's disease, Fabry's disease, Gaucher's disease, and Niemann-Pick disease, are provided. The treatment includes administering to a subject a farnesyl transferase inhibitor compound. The treatment may also include enzyme replacement therapy or gene therapy.
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| 申请人 |
LINK MEDICINE CORPORATION;GRAMMATOPOULOS, TOM, N.;JUSTMAN, CRAIG, J.;LIU, ZHIHUA;LANSBURY, PETER, T.;CULLEN, VALERIE, CHRISTINA |
发明人 |
GRAMMATOPOULOS, TOM, N.;JUSTMAN, CRAIG, J.;LIU, ZHIHUA;LANSBURY, PETER, T.;CULLEN, VALERIE, CHRISTINA |
