The present invention provides a compound which is an inhibitor of sphingolipid biosynthesis for use in the treatment of a disease which has a secondary Niemann-Pick type C disease like cellular phenotype.
申请公布号
EP2182936(A2)
申请公布日期
2010.05.12
申请号
EP20080762509
申请日期
2008.06.26
申请人
THE CHANCELLOR, MASTERS AND SCHOLARS OF THE UNIVERSITY OF OXFORD;THE GOVERNMENT OF THE USA AS REPRESENTED BY THE SECRETARY OF THE DEPARTMENT OF HEALTH& HUMAN SERV.
