发明名称 FOLLISTATIN IN TREATING DUCHENNE MUSCULAR DYSTROPHY
摘要 The present invention provides, among other things, methods and compositions for treating muscular dystrophy, in particular, Duchenne muscular dystrophy (DMD). In some embodiments, a method according to the present invention includes administering to an individual who is suffering from or susceptible to DMD an effective amount of a recombinant follistatin protein such that at least one symptom or feature of DMD is reduced in intensity, severity, or frequency, or has delayed onset.
申请公布号 EP2948161(A1) 申请公布日期 2015.12.02
申请号 EP20140706362 申请日期 2014.01.24
申请人 SHIRE HUMAN GENETIC THERAPIES, INC. 发明人 MINEAU, ROCHELLE
分类号 A61K38/16;A61K38/17;A61P21/00 主分类号 A61K38/16
代理机构 代理人
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