发明名称 METHODS AND COMPOSITIONS FOR TREATING A SERPINC1-ASSOCIATED DISORDER
摘要 The invention relates to iRNA, e.g., double-stranded ribonucleic acid (dsRNA), compositions targeting the Serpinc1 gene, and methods of using such iRNA, e.g., dsRNA, compositions to inhibit expression of Serpinc1 and to treat subjects having a Serpinc1-associated disease, e.g., a bleeding disorder, such as a hemophilia.
申请公布号 WO2015175510(A1) 申请公布日期 2015.11.19
申请号 WO2015US30337 申请日期 2015.05.12
申请人 ALNYLAM PHARMACEUTICALS, INC. 发明人 AKINC, AKIN
分类号 C12N15/113;A61K31/712;A61P7/04 主分类号 C12N15/113
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