发明名称 |
ANTISENSE NUCLEIC ACID |
摘要 |
The purpose of the invention is to provide a drug to produce highly efficient skipping of exons 55 45 50 and 44 of a human dystrophin gene. The invention provides an oligomer that makes it possible to skip exons 55 45 50 and 44 of a human dystrophin gene. |
申请公布号 |
IN6220DEN2014(A) |
申请公布日期 |
2015.10.23 |
申请号 |
IN2014DELNP6220 |
申请日期 |
2014.07.23 |
申请人 |
NIPPON SHINYAKU CO. LTD.;NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY |
发明人 |
WATANABE NAOKI;SEO HARUNA;TAKEDA SHINICHI;NAGATA TETSUYA |
分类号 |
C12N15/113;A61K31/708;A61K48/00 |
主分类号 |
C12N15/113 |
代理机构 |
|
代理人 |
|
主权项 |
|
地址 |
|