发明名称 ANTISENSE NUCLEIC ACID
摘要 The purpose of the invention is to provide a drug to produce highly efficient skipping of exons 55 45 50 and 44 of a human dystrophin gene. The invention provides an oligomer that makes it possible to skip exons 55 45 50 and 44 of a human dystrophin gene.
申请公布号 IN6220DEN2014(A) 申请公布日期 2015.10.23
申请号 IN2014DELNP6220 申请日期 2014.07.23
申请人 NIPPON SHINYAKU CO. LTD.;NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY 发明人 WATANABE NAOKI;SEO HARUNA;TAKEDA SHINICHI;NAGATA TETSUYA
分类号 C12N15/113;A61K31/708;A61K48/00 主分类号 C12N15/113
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