发明名称 MODULATION OF RNA BY REPEAT TARGETING
摘要 Disclosed herein are antisense compounds, compositions and methods for modulating an RNA target by targeting a repetitive sequence in the RNA target and modulating an associated disease, disorder and/or condition related to such RNA target. Also disclosed herein are methods of identifying such compounds and compositions.
申请公布号 EP2812342(A4) 申请公布日期 2015.10.21
申请号 EP20130746752 申请日期 2013.02.08
申请人 ISIS PHARMACEUTICALS, INC. 发明人 FREIER, SUSAN, M.
分类号 C07H21/04;C12N15/11 主分类号 C07H21/04
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