发明名称 Small molecule conjugates for intracellular delivery of biologically active compounds
摘要 The invention provides novel compounds and conjugates of these compounds useful for the delivery of biologically active substances. Further novel design criteria for chemically stabilized siRNA particular useful when covalently attached to a delivery polymer to achieve in vivo mRNA knock down are disclosed therein.
申请公布号 US2014135381(A1) 申请公布日期 2014.05.15
申请号 US201313917524 申请日期 2013.06.13
申请人 HOFFMANN-LA ROCHE INC. 发明人 HADWIGER PHILIPP;HOFFMANN TORSTEN;JAHN-HOFMANN KERSTIN;KITAS ERIC A.;LEWIS DAVID L.;MOHR PETER;MUELLER HANS MARTIN;OTT GUENTHER;ROEHL INGO;ROZEMA DAVID B.
分类号 A61K47/48;A61K31/7088 主分类号 A61K47/48
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