发明名称 |
MOLECULES CHIMIQUES INHIBITRICES DU MECANISME D'EPISSAGE POUR TRAITER DES MALADIES RESULTANT D'ANOMALIES D'EPISSAGE. |
摘要 |
The present invention relates to a compound of one of the formulas I to XXI; a pharmaceutical composition comprising at least one such compound; and the use of at least one such compound in preparing a drug to treat, in a subject, a genetic disease resulting from at least one splicing anomaly. |
申请公布号 |
FR2983200(B1) |
申请公布日期 |
2015.09.25 |
申请号 |
FR20130050601 |
申请日期 |
2013.01.24 |
申请人 |
CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE;INSTITUT CURIE;UNIVERSITE MONTPELLIER 2 SCIENCES ET TECHNIQUES |
发明人 |
TAZI JAMAL;GRIERSON DAVID;MAHUTEAU-BETZER FLORENCE |
分类号 |
C07D401/12;A61K31/4409;A61K31/4439;A61P19/00;A61P25/00;A61P31/18;A61P35/00;C07D213/53;C07D249/06 |
主分类号 |
C07D401/12 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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