发明名称 MOLECULES CHIMIQUES INHIBITRICES DU MECANISME D'EPISSAGE POUR TRAITER DES MALADIES RESULTANT D'ANOMALIES D'EPISSAGE.
摘要 The present invention relates to a compound of one of the formulas I to XXI; a pharmaceutical composition comprising at least one such compound; and the use of at least one such compound in preparing a drug to treat, in a subject, a genetic disease resulting from at least one splicing anomaly.
申请公布号 FR2983200(B1) 申请公布日期 2015.09.25
申请号 FR20130050601 申请日期 2013.01.24
申请人 CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE;INSTITUT CURIE;UNIVERSITE MONTPELLIER 2 SCIENCES ET TECHNIQUES 发明人 TAZI JAMAL;GRIERSON DAVID;MAHUTEAU-BETZER FLORENCE
分类号 C07D401/12;A61K31/4409;A61K31/4439;A61P19/00;A61P25/00;A61P31/18;A61P35/00;C07D213/53;C07D249/06 主分类号 C07D401/12
代理机构 代理人
主权项
地址