| 摘要 |
<p>H:/imt/Intenvovcn/NRPortbl/DCC/AMT/8305733_l.docx-24/08/2015 The present invention provides treating LAL deficiency (e.g. Wolman's disease, CESD) comprising administering to a mammal a therapeutically effective amount of lysosomal acid lipase with an effective dosage frequency. Methods of improving growth and liver function, increasing LAL tissue concentration, and increasing LAL activity in a human patient suffering from LAL deficiency are also provided.</p> |
